Rehabilitation in Muscular Dystrophies: Changing Approach
نویسندگان
چکیده
Life expectancy is increasing in muscular dystrophies: as an example due to technical medical interventions like spine surgery and home ventilation, boys with Duchenne muscular dystrophy become men. Increasing evidence concerning retarding drugs becomes available for muscular dystrophies. Cardiac symptoms can effectively be treated with drugs and also cardioprotective drugs are tested. New retarding treatments, like exon skipping, stem cell treatment or vector-gene transfer, are in the phase of animal studies or already in randomized clinical trials. Together these treatments are changing the course of the muscular dystrophies.
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